New UK collaboration provides hope of gene therapy for liver condition
A new collaboration between Children’s Medical Research Institute (CMRI) and Bloomsbury Genetic Therapies Limited (Bloomsbury), a clinical-stage biotechnology company based in the UK, could see a novel gene therapy for a devastating genetic liver metabolic condition enter clinical trials within months – providing hope for children who currently have to undergo liver transplantation to survive.…
World first trial for kids with Duchenne muscular dystrophy
Exciting news today about the world-first delivery of a gene therapy at Westmead.
Cost of going blind calculated for first time as $5.2m
Researchers have for the first time calculated the lifetime cost of living with an inherited eye disease in Australia as $5.2 million per person. Distressingly, a significant portion of the cost associated with the progressive loss of vision is absorbed by the individuals affected and their families, with over one-third of these costs being due…
Prestigious national award for Professor Ian Alexander
A pioneer of the Australian gene therapy field, Professor Ian Alexander, has been awarded the prestigious Peter Wills Medal as part of the Research Australia Health and Medical Research Awards. Professor Alexander is head of Children’s Medical Research Institute’s Gene Therapy Research Unit, which he founded over 25 years ago, as a joint initiative with…
Loading…
Something went wrong. Please refresh the page and/or try again.
Get new content delivered directly to your inbox.